Biomarkers for Immunotherapy


As rapid development of novel immunotherapies continues, there is enormous pressure to discover and validate relevant biomarkers. Cambridge Healthtech Institute’s Inaugural Biomarkers for Immunotherapy conference has been designed to support a coordinated effort by industry players to discover biomarkers that will enable commercial immunotherapies and immunotherapy combinations through clinical development and into the market. Key focus will be given to combination therapies, biomarkers beyond PD-1, and ensuring safety. Overall, this event will provide solutions and strategies for integrating immunotherapies into the precision medicine model.

Final Agenda

WEDNESDAY, 12 APRIL

12:30 Registration

Emerging Immuno-Oncology Biomarkers and Approaches

13:30 Chairperson’s Opening Remarks

Shao-An Xue, Ph.D., Genetic Engineering Laboratory, School of Biological & Environmental Engineering, Xi’an University, Institute of Immunity & Transplantation, University College London Medical School, United Kingdom

13:35 Cytomegalovirus and Epstein-Barr Virus, Two Unique Biomarkers for Immunotherapy of the Virally Associated Malignancies

Shao-An_XueShao-An Xue, Ph.D., Genetic Engineering Laboratory, School of Biological & Environmental Engineering, Xi’an University, Institute of Immunity & Transplantation, University College London Medical School, United Kingdom

Using CMV and EBV as biomarkers, we isolated HLA-A2-restricted TCR genes specific for CMV and EBV, and retrovirally transduced them into human T cells, thus generated MHC class I-restricted both CD8+ and CD4+ T cells specific for these viruses. This talk will describe a robust approach for generating CD8+ CTL and CD4+ Th cells capable of providing MHC class I-restricted antitumor immunity by targeting CMV and EBV as biomarkers.

14:05 Biomarkers for Early Phase Immune-Oncology Trials

Sidath_KatugamplaSid Katugampola, Ph.D., Biomarker & Translational Scientist, Centre for Drug Development, Cancer Research UK, United Kingdom

Numbers of immunotherapeutic anti-cancer therapies are on the rise and these are showing promising anti-tumour efficacy. Successful translation of these agents and understanding if and how these would work clinically, particularly for first in class (FIC), are of great importance. The use of pharmacodynamic biomarkers in early phase clinical development for such FIC agents provide exciting opportunities but also significant challenges in trials done on late stage cancer patients.

14:35 PD-L1 Expression in HPV Related Cancer: A Multiparameter Biomarker Approach

Ekaterina_KuznetsovaEkaterina S. Jordanova, Ph.D., Principle Investigator, Obstetrics and Gynaecology, Centre for Gynaecological Oncology Amsterdam, The Netherlands

Expression of PD-L1 is still a controversial biomarker for selecting patients for PD1/PD-L1 checkpoint inhibitor immunotherapy. In virally induced tumours such as cervical-, penile-, vulvar-, and head-and-neck cancer various immunotherapy clinical trials are being currently planned or performed. We have recently reported on the link between PD-L1 expression in cervical-, penile- and head-and-neck cancer with poor prognosis. We have developed a multiparameter immunofluorescent technique allowing the analysis of PD-L1 expression in combination with other crucial immune-microenvironment markers. Conceivably, in the near future patients might be easily stratified for particular personalized immunotherapies based on comparable approaches.

15:15 Refreshment Break in the Exhibit Hall with Poster Viewing


16:15 KEYNOTE PRESENTATION: Precision Immunotherapy: The Challenge of Converting Complex Predictive Biomarkers into Practical Companion Diagnostics

Kenneth EmancipatorKenneth Emancipator M.D., Executive Medical Director, Translational Medicine, Companion Diagnostics, Merck & Co., United States

Early immunotherapies have produced dramatic results for some patients, but future immunotherapies likely need to be guided by diagnostics to benefit more patients. Properly targeting immunotherapy requires incorporating into clinical practice complex diagnostics which can assess host immune response in addition to cancer biology itself. “Precision Immunotherapy” requires discovery of appropriate predictive biomarkers and incorporating them into practical companion diagnostics which will be adopted by practitioners.

DRUG RESISTANCE

16:45 Immunostimulatory and Oncolytic Properties of Rotavirus Can Overcome Resistance to Immune Checkpoint Blockade Therapy.

Tala_ShekarianTala Shekarian, Targeting of Tumor and It's Immune Environments, Lyon Cancer Center, France

Oncolytic properties of viruses can be exploited for the priming of anti-tumor immune responses. We have found that commercially available rotavirus vaccines do have oncolytic properties. This attenuated virus can directly kill cancer cells. They have pro-inflammatory properties and activate the NF-Kb pathway in a toll-like receptor and IRF3 independent manner. Interestingly, in immunocompetent murine tumor models, intra-tumoral rotavirus overcome resistance and synergize with immune checkpoint targeted therapy.

17:15 Engineering 2nd Generation SPEAR™-T Cells to Overcome TGF-β-Mediated Immunosuppression for Adoptive Cell Therapy

Jonathan SilkJonathan Silk, Ph.D., Group Leader, Cellular Biology, Adaptimmune Ltd, United Kingdom

Adoptive Cell therapy with NY-ESO SPEAR-T cells, is showing promising initial clinical responses in clinical trials for solid and liquid tumors. However, the depth and durability of responses may be affected by inhibitory cytokines such as Transforming Growth Factor-β (TGF-β). We investigated whether SPEAR-T cells engineered to express a dominant negative TGF-β receptor (dnTGFβRII) were resistant to the inhibitory effects of TGF-β in vitro.

17:45 Close of Day

THURSDAY, 13 APRIL

BIOMARKERS FOR MONITORING PATIENTS

08:30 Registration and Morning Coffee

09:00 Chairperson’s Remarks

Thomas O. Kleen, Ph.D., Executive Vice President, Immune Monitoring, Epiontis GmbH, Germany

09:05 Next-Generation Immune Monitoring Tools for Immuno-Oncology Trials and Biomarker Discovery- Reducing Sample Amounts and Simplifying Logistics

Thomas_KleenThomas O. Kleen, Ph.D., Executive Vice President, Immune Monitoring, Epiontis GmbH, Germany

Current and next generation Immunotherapy trials now can be monitored with epigenetic-based, quantitative real-time PCR assisted cell counting (qPACC). Samples can be simply frozen and easily shipped without burden on clinical sites, allowing precise and robust quantification of immune cells in all human samples from only 75ul-250ul of whole blood or small amounts of tissue. Regulatory T cells (Tregs), Th17, Tfh, CD3+, CD4+, CD8+, B, NK and PD-1 positive cells are the first examples of a next generation tools for immune monitoring immuno-oncology trials and biomarker discovery.

09:35 Profiling of Immunity Biomarkers in Whole Blood

Alex_ChenchikAlex Chenchik, Ph.D., Scientific Director, Cellecta, Inc., United States

For unbiased discovery of predictive and prognostic biomarkers, we have developed a targeted RNA expression assay that profiles 19,000 genes based on multiplex RT-PCR followed by NGS in whole blood samples stabilized in PAXgene. In this study, we present the performance of the assay for immunophenotyping of immune cells in blood samples from TNBC and sepsis patients and assess the immune responses to complex immunomodulatory stimuli in ex vivo model system.

10:05 Post Translationally Modified Auto-Antigens a Biomarker For Early Diagnosis of Autoimmune Disease

Ahuva_NissimAhuva Nissim, Reader, Antibody and Therapeutic Engineering, Biochemical Pharmacology, Queen Mary University, United Kingdom

Oxidative stress might be a critical player in the parthenogenesis of inflammatory autoimmune diseases. This include Rheumatoid arthritis and type 1 diabetes. Our data shows that in both disease the tissue specific auto-antigens are infect auto-antigens that have been post-translationally modified by oxidants present in the diseased tissue. We have shown specific reactivity to oxidated collagen type II and insulin in rheumatoid arthritis and type 1 autoimmune diabetes, respectively.

10:35 Coffee Break in the Exhibit Hall with Poster Viewing

11:20 Loss of Immune Recognition by Aberrant Expression of HLA Class I Antigens in Tumors

Barbara SeligerBarbara Seliger, Ph.D., Professor and Director, Medical Immunology, Martin Luther University Halle-Wittenberg, Germany

MHC class I abnormalities occur in a high frequency of tumors of distinct origin and are often associated with worse prognosis and reduced patients’ survival. The underlying molecular mechanism of these deficiencies are diverse and include total, haplotype, allelic loss or downregulation of HLA class surface antigens, or deregulation of major components of component of the MHC class I antigen processing machinery mediated by either transcriptional, epigenetic or posttranscriptional control.

11:50 Monitoring Immune Dysfunction in the Leukemia Microenvironment

Sergio_RutellaSergio Rutella, M.D., Ph.D., Professor, Cancer Immunotherapy, John van Geest Cancer Research Centre, College of Science and Technology, Nottingham Trent University, United Kingdom

Escape from immune surveillance is a hallmark of cancer. The dysfunction of T cells, NK cells and dendritic cells (DC) contribute to defective anti-leukemia responses. IFN-γ-inducible targets expressed by tumor and/or microenvironmental cells, such as indoleamine 2,3-dioxygenase-1, arginase-II, HLA-G and PD-L1, favour T-cell suppression, inhibition of NK-cell function and DC maturation arrest. Strategies are being developed to tackle the above immune suppressive circuits with the aim to improve clinical outcome.

12:20 Sponsored Presentation (Opportunity Available)

12:50 Luncheon Presentation (Sponsorship Opportunity Available) or Enjoy Lunch on Your Own

13:20 Session Break

BIOMARKERS FOR COMBINATION THERAPIES

14:20 Chairperson’s Remarks

Dirk Brockstedt, Ph.D., Senior Vice President, R&D, Aduro BioTech Inc., United States

14:25 Anticipating, Detecting and Treating Immune-Related Toxicity: A Challenge for Combinatorial Immunotherapy

Ioannis_KarydisIoannis Karydis, Ph.D., Associate Professor, Oncology, Cancer Sciences, University of Southampton, United Kingdom

Tumour immunotherapy is coming of age, with a rising number of agents gaining regulatory approval. However, in most cases single agent response rates remain typically well below 40%. Combinatorial immunotherapy offers a chance to dramatically improve on this, at the cost of significant multi-system toxicity. This talk will discuss the issues involved in anticipating, detecting and managing immune-related side effects and outline possible mitigation strategies.

14:55 Novel Immune Monitoring and Biomarker Technologies to Support the Development of Combination Immunotherapies for the Treatment of Cancer.

Dirk_BrockstedtDirk Brockstedt, Ph.D., Senior Vice President, R&D, Aduro BioTech Inc., United States

The approval of several immunotherapies including cancer vaccines and immune checkpoint inhibitors has not only transformed patient’s lives but also brought challenges to the conventional drug development paradigm and the use of typical PK/PD markers to identify optimal patient populations as well as dose level and schedule. This talk will discuss novel immune monitoring and biomarker technologies that were applied for the development of Aduro’s Listeria-based cancer immunotherapy for pancreatic cancer and mesothelioma.

CLINICAL CASE STUDY

15:25 Hormone-Immunotherapy in Endocrine-Dependent Metastatic Breast Cancer: Laboratory and Clinical Data

Andrea_NicoliniAndrea Nicolini, M.D., Clinical Researcher, Internal Medicine, University of Pisa, Italy

Hormone therapy is currently advised for ER+ metastatic breast cancer patients however in most of them the arising of resistance is a not yet well understood hurdle to overcome. We hypothesized that in these patients during clinical benefit from antiestrogen therapy the addition of cycles of sequential immunotherapy could prolong the benefit and delay the occurrence of acquired hormone resistance. In order to validate this hypothesis, in 1992 we started an open, prospective exploratory clinical trial. Here we summarize and update the clinical data and focus on the main serum biomarkers that proved helpful to monitor the efficacy of hormone immune therapy

16:10 Extended Q&A with Session Speaker

16:25 Refreshment Break

CHALLENGES FOR FUTURE BIOMARKER DISCOVERY

16:45 CLOSING PANEL: Strategies for Practical Application of Biomarker Research

Moderator:
Dirk_BrockstedtDirk Brockstedt, Ph.D., Senior Vice President, R&D, Aduro BioTech Inc., United States


Shao-An_XueShao-An Xue, Ph.D., Genetic Engineering Laboratory, School of Biological & Environmental Engineering, Xi’an University, Institute of Immunity & Transplantation, University College London Medical School, United Kingdom


Ekaterina S. Jordanova, Ph.D., Principle Investigator, Obstetrics and Gynaecology, Centre for Gynaecological Oncology Amsterdam, The Netherlands

Ken_EmancipatorKenneth Emancipator M.D., Executive Medical Director, Translational Medicine, Companion Diagnostics, Merck & Co., United States


  • Sample quality, quantity, and type
  • Standardizing procedures and assay validation
  • Funding, resources, and collaboration

17:45 Close of Conference